melphalan

Overview

Melphalan (L-phenylalanine mustard) is a bifunctional alkylating agent that cross-links DNA. It is used in high-dose autologous stem-cell transplant conditioning (principally in multiple myeloma) and has been evaluated in reduced-intensity allogeneic conditioning regimens for AML and MDS.

Evidence in the corpus

  • Referenced as a component of conditioning regimens for allogeneic SCT in the context of the WashU decitabine AML/MDS trial (NCT01687400, N=116); allogeneic SCT vs no SCT was the dominant Cox survival predictor (P<0.001), and benefit was not adversely affected by TP53 status PMID:27959731

Resistance mechanisms

  • Not specifically reported in the corpus.

Cancer types (linked)

  • AML — reduced-intensity or myeloablative conditioning for allo-SCT.
  • MDS — conditioning for allo-SCT as consolidation after HMA response.

Sources

  • PMID:27959731 — Welch et al. 2016, NEJM. WashU AML/MDS decitabine trial; melphalan referenced as SCT conditioning context; SCT was the dominant survival predictor.

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